DelveInsight’s, “Rett Syndrome Pipeline Insight 2023” report provides comprehensive insights about 20+ companies and 20+ pipeline drugs in the Rett Syndrome pipeline landscape. It covers the Rett Syndrome pipeline drug profiles, including Rett Syndrome clinical trials and nonclinical stage products. It also covers the Rett Syndrome therapeutics assessment by product type, stage, route of administration, and molecule type. It further highlights the inactive pipeline products in this space.
Latest Developmental Activities in the Rett Syndrome Treatment Landscape
Discover the recent breakthroughs happening in the Rett Syndrome Pipeline landscape @ Rett Syndrome Pipeline Outlook
Key Takeaways from the Rett Syndrome Pipeline Report
Rett Syndrome Emerging Drugs Profile
Trofinetide (previously designated by Neuren as NNZ-2566) and NNZ-2591 are patented synthetic analogs of molecules which are derived from IGF-1 and occur naturally in the brain. IGF-1 is a growth factor stimulated by growth hormone. In the central nervous system, IGF-1 is produced by both of the major types of brain cells – neurons and glia. IGF-1 in the brain is critical both for normal development and for responding to injury and disease. . The US Food and Drug Administration (FDA) and the European Medicines Agency (EMA) have both granted Orphan Drug designation to Neuren for trofinetide in Rett syndrome. The FDA has also granted Fast Track designation. The drug also has a Rare Pediatric Disease designation. Neuren’s North American partner for trofinetide, ACADIA Pharmaceuticals, has announced positive top-line results from a Phase III trial in Rett syndrome.Neuren Pharmaceuticals reported that the US Food and Drug Administration (FDA) has accepted for review the New Drug Application (NDA) of trofinetide for the treatment of Rett syndrome, that was submitted by Neuren’s US partner Acadia Pharmaceuticals (Nasdaq: ACAD). The FDA had granted a Priority Review and assigned a Prescription Drug User Fee Act (PDUFA) action date of 12 March 2023.
ANAVEX2-73 (blarcamesine) activates the Sigma-1 receptor (S1R) protein, which serves as a molecular chaperone and functional modulator involved in restoring cellular homeostasis. The drug is in phase III stage of clinical trial evaluation for the treatment of patients with Rett syndrome.
Get More Information on the Rett Syndrome Drugs and Companies of Report @ Rett Syndrome Ongoing Clinical Trials Analysis
Scope of the Rett Syndrome Pipeline Report
Find out more about the list of FDA-approved drugs for Rett Syndrome @ Rett Syndrome Treatment Landscape
Table of Content
Got Queries? Find out the related information on Rett Syndrome Preclinical and Discovery Stage Products @ Rett Syndrome Drugs, Unmet Needs and Recent Trends
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